Table 1

Patient diagnoses and bone marrow transplant details

Patient Phenotype Molecular diagnosis Age at BMT Type of BMT Conditioning regimen Admission
length (days)
Time after last BMT (years) Chimerism (T/B)
1TB+ cgc68 daysHaplo TCDBu8;Cy20022611.5D/mixed
2TB+NK+ Unknown38 daysHaplo TCDBu8;Cy2002067.3D/D
3TB+NK+ Unknown35 daysHaplo TCDBu8;Cy2002106.7D/R
4TB−NK+ Unknown48 daysPheno WholeNil192
2 years 5 monthsPheno WholeNil163D/mixed
5TB+NK+ Unknown58 daysHaplo TCDBu8;Cy200;ATG61714.8D/mixed
6TBNK ADA93 daysURD TCDBu16;Cy2002304.3D/mixed
7TBNK Unknown66 daysURD TCDBu8;Cy200201
Radiosensitive302 daysURD TCDNil214
2.5 yearsHaplo TCDBu16;Cy200;ATG61571.5D/Unknown
8TB+NK+ Unknown45 daysHaplo TCDBu8;Cy2001723.2D/R
9TBNK+ RAG241 daysHaplo TCDBu8;Cy200144
1 year 5 monthsHaplo TCDNil1
2 years 1 monthHaplo TCDBu16;Cy200640.5D/Unknown
10TBNK ADA39 daysSib WholeNil582.3D/mixed
11TBNK ADA33 daysSib WholeNil832D/mixed
12TBNK+ Unknown7 daysSib Cord BloodNil561.6D/mixed
13TB+ cgc45 daysHaplo TCDBu8;Cy2001681.3D/R
  • cgc, Common interleukin gamma chain deficiency; ADA, adenosine deaminase deficiency; RAG2, recombination activation gene 2 deficiency; Haplo, haplo-identical; TCD, T cell depleted; Pheno, phenotypic; URD, unrelated donor; Sib, sibling; Bu, busulfan; Cy, cyclophosphamide; ATG, anti-thymocyte globulin; BMT, bone marrow transplant; T/B, T lymphocytes/B lymphocytes; D, donor; R, recipient.