Patient | Phenotype | Molecular diagnosis | Age at BMT | Type of BMT | Conditioning regimen |
Admission length (days) | Time after last BMT (years) | Chimerism (T/B) | |||
1 | T−B+ | cgc | 68 days | Haplo TCD | Bu8;Cy200 | 226 | 11.5 | D/mixed | |||
2 | T−B+NK+ | Unknown | 38 days | Haplo TCD | Bu8;Cy200 | 206 | 7.3 | D/D | |||
3 | T−B+NK+ | Unknown | 35 days | Haplo TCD | Bu8;Cy200 | 210 | 6.7 | D/R | |||
4 | T−B−NK+ | Unknown | 48 days | Pheno Whole | Nil | 192 | |||||
2 years 5 months | Pheno Whole | Nil | 16 | 3 | D/mixed | ||||||
5 | T−B+NK+ | Unknown | 58 days | Haplo TCD | Bu8;Cy200;ATG6 | 171 | 4.8 | D/mixed | |||
6 | T−B−NK− | ADA | 93 days | URD TCD | Bu16;Cy200 | 230 | 4.3 | D/mixed | |||
7 | T−B−NK− | Unknown | 66 days | URD TCD | Bu8;Cy200 | 201 | |||||
Radiosensitive | 302 days | URD TCD | Nil | 214 | |||||||
2.5 years | Haplo TCD | Bu16;Cy200;ATG6 | 157 | 1.5 | D/Unknown | ||||||
8 | T−B+NK+ | Unknown | 45 days | Haplo TCD | Bu8;Cy200 | 172 | 3.2 | D/R | |||
9 | T−B−NK+ | RAG2 | 41 days | Haplo TCD | Bu8;Cy200 | 144 | |||||
1 year 5 months | Haplo TCD | Nil | 1 | ||||||||
2 years 1 month | Haplo TCD | Bu16;Cy200 | 64 | 0.5 | D/Unknown | ||||||
10 | T−B−NK− | ADA | 39 days | Sib Whole | Nil | 58 | 2.3 | D/mixed | |||
11 | T−B−NK− | ADA | 33 days | Sib Whole | Nil | 83 | 2 | D/mixed | |||
12 | T−B−NK+ | Unknown | 7 days | Sib Cord Blood | Nil | 56 | 1.6 | D/mixed | |||
13 | T−B+ | cgc | 45 days | Haplo TCD | Bu8;Cy200 | 168 | 1.3 | D/R |
cgc, Common interleukin gamma chain deficiency; ADA, adenosine deaminase deficiency; RAG2, recombination activation gene 2 deficiency; Haplo, haplo-identical; TCD, T cell depleted; Pheno, phenotypic; URD, unrelated donor; Sib, sibling; Bu, busulfan; Cy, cyclophosphamide; ATG, anti-thymocyte globulin; BMT, bone marrow transplant; T/B, T lymphocytes/B lymphocytes; D, donor; R, recipient.